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Long-Term Follow-up Study for RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)

1d agoen
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Conditions : SHANK3 Haploinsufficiency; Phelan-McDermid Syndrome Interventions : Biological: RB001 Sponsors : Peking University First Hospital; Shenzhen Reborngene Therapeutics Co., Ltd. Enrolling by invitation
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