The Latest Data from Lenadogene Nolparvovec Gene Therapy Trials for Leber Hereditary Optic Neuropathy - Part 3
In part two of this four-part series, Dr. Justin Abbatemarco and Dr. Nancy Newman discuss current treatment options for Leber hereditary optic neuropathy (LHON). Show reference
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Saffie Sandford from Stevenage was diagnosed with Leber's Congenital Amaurosis, (LCA) a mutation in the RPE 65 gene.
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