FDA Drug Approval Affects Healthcare Around the World, but Political Shortcuts Could Hurt the Agency’s International Reputation

Gene therapy for children with sickle cell disease approved by FDA

A new treatment for children aged 2 or older with sickle cell disease has been approved by the U.S. Food & Drug Administration.

FDA Approves First Gene Therapy For Young Children With Sickle Cell Disease

The report said a clinical trial involving 15 children between the ages of 5 and 11 produced encouraging results.

CRISPR gene therapy insights may improve access to sickle cell cures

Amazing News! This is a cost effective treatment of sickle cell disease. Recall that Jennifer Doudna & Emmanuelle Charpentier shared the Nob

<![CDATA[FDA Expands Casgevy Approval to Children as Young as 2 Years With Sickle Cell Disease or Transfusion-Dependent β-Thalassemia]]>

The Inquiry

Can gene therapy become accessible for people living with sickle cell disease?

HCA Healthcare announces New England Journal of Medicine study highlighting advances in CRISPR-based therapy for children

Today, HCA Healthcare is proud to announce new research published in The New England Journal of Medicine (NEJM) demonstrating promising resu