Equity in the age of advanced therapies: insights from haemophilia
In Laurence Woollard's latest blog for Rare Disease Day, he reflects on how advanced therapies are being introduced within the NHS – highlighting the need for a Patient Charter.
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Patient reflects on decades of progress in sickle cell treatment
Audrey Smith, 78, was diagnosed with sickle cell disease at a young age; she has received care at Johns Hopkins for more than 20 years
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Audrey Smith, 78, was diagnosed with sickle cell disease at a young age; she has received care at Johns Hopkins for more than 20 years
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CME Event: From Treatment Advances to Individualized Care in Hemophilia - August 2026
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