FDA Approves Ultragenyx Gene Therapy for Rare Sanfilippo Syndrome Type A

5 articles · 4 sources · updated 4 hours ago

Recent

bizjournals.comFDA Approves Ultragenyx Gene Therapy for Rare Sanfilippo Syndrome Type A4 hours ago

0

Asianet NewsableRARE Stock Jumps 13% — Extends Gains After-Hours As FDA Clears First Sanfilippo Gene Therapy9 hours ago · By Stocktwits Inc

0

STATSTAT+: FDA approves a new gene therapy for Sanfilippo syndrome, an ultra-rare disease13 hours ago · By Jason Mast

0

Radiological Society of North AmericaUltragenyx wins FDA nod for Sanfilippo gene therapy13 hours ago

0

Asianet NewsableRARE Stock Hits Fresh 52-Week Low As Sanfilippo Drug Ruling Nears — Failed Angelman Syndrome Trial Weighs On Shares1 days ago · By Stocktwits Inc

0

Posts from social

Ron Leuty@rleutybiotech.bsky.socialUltragenyx's $4 million gene therapy wins FDA approval for a rare brain and nervous system disorderPosted on Bluesky· 4 hours ago