https://doi.org/10.1056/NEJMoa2504835
2h ago
Risto-cel edits HBG1/2 promoters in CD34⁺ cells, boosting HbF to counteract SCD symptoms. Phase 1-2 results promising for relief! PMID:41931046, N Engl J Med 2026, @NEJM https://doi.org/10.1056/NEJMoa2504835 #Medsky #Pharmsky #RNA #ASHG #ESHG 🧪
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